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Indications and Purposes

1 Indications And Usage Luxturna (Voretigene Neparvovec-Rzyl) Is An Adeno-Associated Virus Vector-Based Gene Therapy Indicated For The Treatment Of Patients With Confirmed Biallelic Rpe65 Mutation-Associated Retinal Dystrophy. Patients Must Have Viable Retinal Cells As Determined By The Treating Physician(S). Luxturna Is An Adeno-Associated Virus Vector-Based Gene Therapy Indicated For The Treatment Of Patients With Confirmed Biallelic Rpe65 Mutation-Associated Retinal Dystrophy. Patients Must Have Viable Retinal Cells As Determined By The Treating Physician(S). ( 1 )

All Formulated Excipients (0 Total)

None

Active Ingredients ( 1 Total)

Name Structure ZINC ID(s)
1. Voretigene Neparvovec-Rzyl

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