Application Nr Approved Date Route Status External Links
BLA761052 None Intraventricular None Google , Wikipedia , PubMed , DailyMed , Raw OpenFDA , ECHA , ToxNet , JECFA , FAO , 21 CFR

Indications and Purposes

1 Indications And Usage Brineura Is Indicated To Slow The Loss Of Ambulation In Symptomatic Pediatric Patients 3 Years Of Age And Older With Late Infantile Neuronal Ceroid Lipofuscinosis Type 2 (Cln2), Also Known As Tripeptidyl Peptidase 1 (Tpp1) Deficiency. Brineura Is A Hydrolytic Lysosomal N-Terminal Tripeptidyl Peptidase Indicated To Slow The Loss Of Ambulation In Symptomatic Pediatric Patients 3 Years Of Age And Older With Late Infantile Neuronal Ceroid Lipofuscinosis Type 2 (Cln2), Also Known As Tripeptidyl Peptidase 1 (Tpp1) Deficiency. ( 1 )

All Formulated Excipients (0 Total)

None

Active Ingredients ( 1 Total)

Name Structure ZINC ID(s)
1. Cerliponase Alfa

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